By Steve Lundeberg – Oregon State University –
by overcoming the challenge of consistently getting genes and gene-editing tools where they need to be within cells.
Findings of the study spearheaded by Oregon State University College of Pharmacy graduate student Antony Jozić were published today in Nature Biotechnology.
When gene therapies enter a cell, they are often sent to lysosomes, the cell’s trash and recycling centers, where therapeutic genetic material is broken down before it can work. For gene therapies to succeed, they must avoid disposal and reach the part of the cell where they can function.
